Precise gene editing preserves hematopoietic stem cell function following transient p53-mediated DNA damage response G Schiroli, A Conti, S Ferrari, L Della Volpe, A Jacob, L Albano, S Beretta, ... Cell stem cell 24 (4), 551-565. e8, 2019 | 259 | 2019 |
Preclinical modeling highlights the therapeutic potential of hematopoietic stem cell gene editing for correction of SCID-X1 G Schiroli, S Ferrari, A Conway, A Jacob, V Capo, L Albano, T Plati, ... Science translational medicine 9 (411), eaan0820, 2017 | 213 | 2017 |
Efficient gene editing of human long-term hematopoietic stem cells validated by clonal tracking S Ferrari, A Jacob, S Beretta, G Unali, L Albano, V Vavassori, D Cittaro, ... Nature biotechnology 38 (11), 1298-1308, 2020 | 126 | 2020 |
Assessment of ovarian reserve after cystectomy versus ‘one-step’laser vaporization in the treatment of ovarian endometrioma: a small randomized clinical trial M Candiani, J Ottolina, E Posadzka, S Ferrari, LM Castellano, I Tandoi, ... Human Reproduction 33 (12), 2205-2211, 2018 | 89 | 2018 |
Choice of template delivery mitigates the genotoxic risk and adverse impact of editing in human hematopoietic stem cells S Ferrari, A Jacob, D Cesana, M Laugel, S Beretta, A Varesi, G Unali, ... Cell Stem Cell 29 (10), 1428-1444. e9, 2022 | 52 | 2022 |
Gene editing of hematopoietic stem cells: hopes and hurdles toward clinical translation S Ferrari, V Vavassori, D Canarutto, A Jacob, MC Castiello, AO Javed, ... Frontiers in Genome Editing 3, 618378, 2021 | 34 | 2021 |
Genotoxic effects of base and prime editing in human hematopoietic stem cells M Fiumara, S Ferrari, A Omer-Javed, S Beretta, L Albano, D Canarutto, ... Nature biotechnology, 1-15, 2023 | 32 | 2023 |
Mobilization-based chemotherapy-free engraftment of gene-edited human hematopoietic stem cells A Omer-Javed, G Pedrazzani, L Albano, S Ghaus, C Latroche, M Manzi, ... Cell 185 (13), 2248-2264. e21, 2022 | 29 | 2022 |
Genetic engineering meets hematopoietic stem cell biology for next-generation gene therapy S Ferrari, E Valeri, A Conti, S Scala, A Aprile, R Di Micco, ... Cell Stem Cell 30 (5), 549-570, 2023 | 20 | 2023 |
Lipid nanoparticles allow efficient and harmless ex vivo gene editing of human hematopoietic cells V Vavassori, S Ferrari, S Beretta, C Asperti, L Albano, A Annoni, ... Blood 142 (9), 812-826, 2023 | 11 | 2023 |
Mesenchymal stromal cells improve the transplantation outcome of CRISPR-Cas9 gene-edited human HSPCs S Crippa, A Conti, V Vavassori, S Ferrari, S Beretta, S Rivis, R Bosotti, ... Molecular Therapy 31 (1), 230-248, 2023 | 11 | 2023 |
BAR-Seq clonal tracking of gene-edited cells S Ferrari, S Beretta, A Jacob, D Cittaro, L Albano, I Merelli, L Naldini, ... Nature Protocols 16 (6), 2991-3025, 2021 | 10 | 2021 |
Flexible CO2 laser fiber: first look at the learning curve required in gynecological laparoscopy training. VS Vanni, J Ottolina, G Candotti, LM Castellano, I Tandoi, G Poppi, ... Minerva Ginecologica 70 (1), 53-57, 2017 | 8 | 2017 |
Preclinical modeling highlights the therapeutic potential of hematopoietic stem cell gene editing for correction of SCID-X1. Sci Transl Med 2017; 9 G Schiroli, S Ferrari, A Conway, A Jacob, V Capo, L Albano | 6 | |
Correcting inborn errors of immunity: From viral mediated gene addition to gene editing MC Castiello, S Ferrari, A Villa Seminars in Immunology 66, 101731, 2023 | 3 | 2023 |
Exonic knockout and knockin gene editing in hematopoietic stem and progenitor cells rescues RAG1 immunodeficiency MC Castiello, C Brandas, S Ferrari, S Porcellini, N Sacchetti, D Canarutto, ... Science Translational Medicine 16 (733), eadh8162, 2024 | 2 | 2024 |
Unbiased assessment of genome integrity and purging of adverse outcomes at the target locus upon editing of CD4+ T‐cells for the treatment of Hyper IgM1 D Canarutto, C Asperti, V Vavassori, S Porcellini, E Rovelli, M Paulis, ... The EMBO Journal 42 (23), e114188, 2023 | 2 | 2023 |
Scalable GMP-compliant gene correction of CD4+ T cells with IDLV template functionally validated in vitro and in vivo C Asperti, D Canarutto, S Porcellini, F Sanvito, F Cecere, V Vavassori, ... Molecular Therapy-Methods & Clinical Development 30, 546-557, 2023 | 2 | 2023 |
The impact on ovarian reserve of ovarian cystectomy versus laser vaporization in the treatment of ovarian endometrioma: a randomized clinical trial J Ottolina, E Posadzka, S Ferrari, I Tandoi, LM Castellano, J Komenda, ... Journal of Minimally Invasive Gynecology 24 (7), S55-S56, 2017 | 2 | 2017 |
Mobilization-based engraftment of haematopoietic stem cells: a new perspective for chemotherapy-free gene therapy and transplantation D Canarutto, A Omer Javed, G Pedrazzani, S Ferrari, L Naldini British Medical Bulletin 147 (1), 108-120, 2023 | 1 | 2023 |